Cambridge Healthtech Institute’s 5th Annual
RNA-Modulating Small Molecule Drugs
Novel Approaches to Target RNA Structure, Binding, Interactions, and Function
April 3-4, 2024
With an increased understanding of diverse RNA moieties, their structure, function, and interactions, finding small molecules to target RNA is getting simpler. Small molecules offer enhanced stability, oral bioavailability, and better drug-like properties when compared to oligonucleotides. Hence, they are a more viable therapeutic option. However, identifying the right disease-causing RNA and evaluating the downstream physiological responses after small molecule modulation can be quite challenging. Challenges also exist in terms of optimizing the specificity, selectivity, and safety of these small molecules in vivo. Cambridge Healthtech Institute’s conference on RNA-Modulating Small Molecule Drugs will highlight some of the innovative approaches and technologies being used in this field.